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Early Access

Showing 1 - 25 of >10,000

STUDY
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Paroxysmal Nocturnal Hemoglobinuria, PNH, Extravascular Hemolysis Trial (Danicopan)

Available
  • Paroxysmal Nocturnal Hemoglobinuria
  • +2 more
  • (no location specified)
Aug 1, 2023

SLE Patients Treated With Anifrolumab in Early Access Programs

Not yet recruiting
  • Systemic Lupus Erythematosus
  • None (Observational study)
  • (no location specified)
Sep 13, 2023

Wilson Disease Trial (ALXN1840)

Available
  • Wilson Disease
  • (no location specified)
Jan 6, 2023

Locally Advanced Unresectable Gastroesophageal Junction (GEJ) Adenocarcinoma Cancer, Locally Advanced Unresectable Gastric

Available
  • Locally Advanced Unresectable Gastroesophageal Junction (GEJ) Adenocarcinoma Cancer
  • +3 more
  • Morristown, New Jersey
    AMG Hematology/Oncology
Sep 15, 2023

Unresectable Hepatocellular Carcinoma Trial (Durvalumab, Tremelimumab)

Available
  • Unresectable Hepatocellular Carcinoma
  • (no location specified)
Aug 12, 2022

Plantar Fascitis Trial in Cardiff (Early access to virtual resources)

Recruiting
  • Plantar Fascitis
  • Early access to virtual resources
  • Cardiff, United Kingdom
    Clinical research facility
May 17, 2022

Acalabrutinib in Chronic Lymphocytic Leukaemia in United Kingdom

Recruiting
  • Chronic Lymphocytic Leukemia, CLL
  • Aylesbury, United Kingdom
  • +7 more
Jan 12, 2023

Autism Spectrum Disorder Trial in Seattle (Screen-Refer-Treat Intervention)

Completed
  • Autism Spectrum Disorder
  • Screen-Refer-Treat Intervention
  • Seattle, Washington
    University of Washington
Nov 1, 2022

Adult and Pediatric Acid Sphingomyelinase Deficiency on Early

Recruiting
  • Acid Sphingomyelinase Deficiency (ASMD)
  • Olipudase alfa
  • France, France
    Investigational site number France
Jun 13, 2022

Early-stage HER2-positive Breast Cancer, Treated With Neratinib

Recruiting
  • Breast Cancer
  • +2 more
    • Bouge, Belgium
      Clinique Saint-Luc Bouge
    Oct 25, 2022

    Lung Cancer Trial (Lazertinib 240 mg)

    Approved for marketing
    • Lung Cancer
    • Lazertinib 240 mg
    • (no location specified)
    Feb 15, 2022

    Autism Spectrum Disorder, Implementation Science, Mental Health Trial in San Diego (ATTAIN NAV Technology-Enhanced Family

    Recruiting
    • Autism Spectrum Disorder
    • +3 more
    • ATTAIN NAV Technology-Enhanced Family Navigation Model
    • San Diego, California
      UCSD
    Apr 19, 2022

    Atezolizumab Combined With Chemotherapy in Extensive Stage SCLC

    Completed
    • Small Cell Lung Cancer
    • atezolizumab
    • Chalon-sur-Saône, France
    • +1 more
    Jan 5, 2023

    Cholangiocarcinoma Trial in Düsseldorf (Ivosidenib Oral Tablet)

    Recruiting
    • Cholangiocarcinoma
    • Ivosidenib Oral Tablet
    • Düsseldorf, Germany
      Klinik für Gastroenterologie, Hepatologie und Infektiologie Univ
    May 17, 2023

    Peanut Allergy Trial in Madison (DBV712 250 mcg)

    Available
    • Peanut Allergy
    • DBV712 250 mcg
    • Madison, Connecticut
      Early Access Care, LLC
    Jun 14, 2022

    Familial Chylomicronemia Trial (Volanesorsen)

    No longer available
    • Familial Chylomicronemia
    • (no location specified)
    Sep 10, 2021

    Assess Participant-Reported Real-World Experience of

    Recruiting
    • Crohn's Disease
      • London, London, City Of, United Kingdom
        Guys and St Thomas NHS Foundation Trust /ID# 258986
      Nov 7, 2023

      RW Effectiveness of Lurbinectedin in Extensive Stage SCLC

      Completed
      • Small-cell Lung Cancer
      • Paris, France
      • +1 more
      Jan 5, 2023

      Covid19, Vaccines Trial in Westwood (Self-benefit, Prosocial-benefit, Early access)

      Completed
      • Covid19, Vaccines
      • Self-benefit
      • +3 more
      • Westwood, California
        UCLA Health Department of Medicine, Quality Office
      Sep 11, 2022

      Myocardial Infarction Trial in Edmonton, Saskatoon (Early Access CR)

      Suspended
      • Myocardial Infarction
      • Early Access CR
      • Edmonton, Alberta, Canada
      • +1 more
      Nov 4, 2021

      Steroid Resistant Acute GVHD Trial in Lyon (inolimomab)

      Available
      • Steroid Resistant Acute Graft Versus Host Disease
      • inolimomab
      • Lyon, France
        ElsaLys Biotech
      Sep 16, 2021

      Autism Spectrum Disorder Trial in Portland (Autism ALERT, Screening Intervention)

      Active, not recruiting
      • Autism Spectrum Disorder
      • Autism ALERT
      • Screening Intervention
      • Portland, Oregon
        Ohsu Cdrc
      Sep 19, 2022

      Niemann-Pick Disease, Type C Trial in United States (Arimoclomol)

      Available
      • Niemann-Pick Disease, Type C
      • Birmingham, Alabama
      • +14 more
      Aug 18, 2022

      RW Efficacy of Sotorasib in KRAS G12C-mutated Metastatic NSCLC

      Recruiting
      • Nsclc
      • KRAS P.G12C
        • Paris, France
        • +2 more
        Aug 9, 2022

        CENOBAMATE as Adjunctive Treatment in Patients Suffering From

        Recruiting
        • Focal Onset Seizure
        • Epilepsy
          • Bron, France
          • +22 more
          Mar 6, 2023